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Figure 1. Working model of risdiplam mode of action35. ESE: exonic splicing enhancer; mRNA: messenger ribonucleic acid; pre-mRNA: pre-messenger ribonucleic acid; SMN: survival of motor neuron; SMN2: survival of motor neuron 2; ss: splice site.

Figure 1. Working model of risdiplam mode of action35. ESE: exonic splicing enhancer; mRNA: messenger ribonucleic acid; pre-mRNA: pre-messenger ribonucleic acid; SMN: survival of motor neuron; SMN2: survival of motor neuron 2; ss: splice site.

Figure 1. Working model of risdiplam mode of action35. ESE: exonic splicing enhancer; mRNA: messenger ribonucleic acid; pre-mRNA: pre-messenger ribonucleic acid; SMN: survival of motor neuron; SMN2: survival of motor neuron 2; ss: splice site.